Caroline Wall, Hua Xiang, Ben Palmer, Elizabeth Chalmers, Pratima Chowdary, Peter W Collins, Simon Fletcher, Georgina W Hall, Daniel P Hart, Mary Mathias, Paul Sartain, Susan Shapiro, David Stephensen, Kate Talks, Charles R M Hay
INTRODUCTION: The UK National Haemophilia Database (NHD) collects data from all UK persons with haemophilia A with inhibitors (PwHA-I). It is well-placed to investigate patient selection, clinical outcomes, drug safety and other issues not addressed in clinical trials of emicizumab. AIMS: To determine safety, bleeding outcomes and early effects on joint health of emicizumab prophylaxis in a large, unselected cohort using national registry and patient reported Haemtrack (HT) data between 01 January 2018 and 30 September 2021...
February 22, 2023: Haemophilia: the Official Journal of the World Federation of Hemophilia